Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette

A precision-engineered gene therapy virus, inserted into blood stem cells that are then transplanted, markedly reduced sickle-induced red-cell damage in mice with sickle cell disease, researchers from Dana-Farber/Boston Children’s Cancer and Blood Disorders Center reported in the Journal of Clinical Investigation.

Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette

The F.D.A. Approved Gene Editing Therapy for Sickle Cell Disease - The New York Times

New study shows promising evidence for sickle cell gene therapy - UChicago Medicine

Genetic Therapies

Gene correction for sickle cell disease hits its prime

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Health Archives — Page 34 of 107 — Harvard Gazette

Transformative' gene therapies could reduce sickle cell disease complications. Here's how Massachusetts played a part.

Health Archives — Page 34 of 107 — Harvard Gazette

Experimental Gene Therapy Reverses Sickle Cell Disease for Years